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News and Articles
AGC Biologics Partners with Rarity PBC to Advance Life-Saving Gene Therapy for "Bubble Baby Disease"
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Rarity PBC Secures Exclusive License from UCLA TDG to Advance a Life-Saving Gene Therapy for ADA-SCID
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Long-Term Safety and Efficacy of Gene Therapy for Adenosine Deaminase Deficiency
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Donald Kohn awarded $14.7M CIRM grant to advance ADA-SCID gene therapy toward FDA approval
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Donald Kohn awarded $14.7M CIRM grant to advance ADA-SCID gene therapy toward FDA approval
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Gene therapy for ADA-SCID shows promise
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Gene Therapy Brings Hope to Families Affected by Rare Immune Disorder
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Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency
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5-year old with rare disorder awaits gene therapy treatment
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Lunch and Learn: ADA-SCID Gene Therapy Update
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